Characterizing the High Disease Burden of Transthyretin Amyloidosis for Patients and Caregivers

Transthyretin amyloidosis (ATTR amyloidosis), whether manifesting as familial amyloid polyneuropathy (ATTR-PN) or cardiomyopathy (ATTR-CM), is a progressive, debilitating, and often fatal, rare disease requiring significant caregiver support. This study aims to better characterize the burden of disease for ATTR amyloidosis patients and caregivers. Patients and caregivers in the USA and Spain were recruited through patient advocacy groups to...