Using a stated preference discrete choice experiment to assess societal value from the perspective of patients with rare diseases in Italy

Decision makers have huge problems when attempting to attribute social value to the improvements achieved by new drugs, especially when considering the use of orphan drugs for rare diseases. We present the results of a pilot study aimed to investigate patient preferences regarding public funding for drugs used to treat rare diseases. An online questionnaire was used as a discrete choice experiment (DCE) survey to explore the preferences of...